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Session 8: Hot Topics
Session Chair(s)
Emily Place, PHD, MPH
Senior Consultant
Aclairo Pharmaceutical Development Group, United States
Ronald Wange, PHD
Associate Director for Pharm/Tox OND
FDA, United States
Session 8: Hot Topics
Speaker(s)
Presentation Title: Harnessing RNA Exon Editing to Rewrite the Underlying Causes of Genetic Diseases
Robert Bell, PHD
Ascidian, United States
CSO
siRNA Manufacturing with Engineered Enzymes
Stefan Lutz, PHD
Codexis, Inc. , United States
Chief Scientific Officer
Confusion Arising from a Shared Vocabulary: What does “Platform” Really Mean?
Ronald Wange, PHD
FDA, United States
Associate Director for Pharm/Tox OND