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Capital Hilton

2024 年 10 月 28 日 8:30 上午 - 2024 年 10 月 30 日 12:40 下午

1001 16th Street NW, Washington, DC 20036-5794

DIA/FDA Oligonucleotide-Based Therapeutics Conference

Session 2 Track 1: Extra-Hepatic Delivery – Clinical Experience: Emerging

Session Chair(s)

Xing  Jing, PhD, MBA

Xing Jing, PhD, MBA

Reviewer

FDA, United States

Arthur A. Levin, PhD

Arthur A. Levin, PhD

Distinguished Scientist

Avidity Biosciences, United States

Track 1: Extra-Hepatic Delivery – Clinical Experience: Emerging

Speaker(s)

James  Hamilton, MD, MBA

Pulmonary Delivery Platform and Clinical Programs

James Hamilton, MD, MBA

Arrowhead Pharmaceuticals, United States

Chief of Discovery and Transitional Medicine

Thomas  Thum, MD, PhD, FACC

Cardiac Delivery of Oligonucleotides

Thomas Thum, MD, PhD, FACC

Cardior Pharmaceuticals GmbH, Germany

CSO/CMO

Allison  August

Delivery of siRNA to Placenta for Treatment of Preeclampsia

Allison August

Comanche Biopharma, United States

Chief Medical Officer

Steve  Hughes, MD, MBA

Delivery of Oligonucleotides to Muscle in Patients

Steve Hughes, MD, MBA

Avidity Biosciences, United States

Chief Medical Officer

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