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Session Chair(s)
Gopalan Narayanan, MD, FFPM, FRCP
Vice President, Disruptive Biologics
Voisin Consulting Life Sciences, United Kingdom
Speaker(s)
Challenges in Planning a First-in-Man Study with an Advanced Therapy Medicinal Product (ATMP)
Romaldas Maciulaitis
CHMP, CAT, United Kingdom
National Expert
Hematopoietic Stem Cell Gene Therapy for Inherited Disorders: Experience from an Academic Centre
Stefano Zancan
Telethon, Italy
Tiget Clinical Trial Coordinator, Head of Clinical Development
Gene Therapy for Leber Hereditary Optic Neuropathy: From Concept to Pivotal Trials
Jean-Philippe A Combal, PHARMD, PHD
GenSight Biologics, France
Chief Operating Officer