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Session Chair(s)
Sam Wadsworth, PHD
Chief Scientific Officer
Dimension Therapeutics, United States
Speaker(s)
Gene Therapy- A New Treatment Modality- Opportunities and Challenges from a Regulatory Perspective
Marcel Hoefnagel, DRSC, PHD, MSC
Medicines Evaluation Board , Netherlands
Senior Assessor Biopharmaceuticals
Gene Therapy – The Patient’s Perspective
Dimitrios Athanasiou, MBA
WORLD DUCHENNE ORGANIZATION (WDO) , MDA HELLAS, Greece
Patient Advocate
Challenges in Bringing New Treatment Modalities to Patients
Deya Corzo
UniQure, United States
SVP, Therapeutic Area Head
Adaptive Biomedical Innovation – A Supportive Framework for Accelerating the Development of Gene Therapy Products
Anne-Virginie L. Eggimann, MS
bluebird bio, Inc., United States
Chief Regulatory Offcer