Already a DIA Member? Sign in. Not a member? Join.

Sign in

Forgot User ID? or Forgot Password?

Not a Member?

Create Account and Join

Online

Rare Diseases Webinar Series: Part 3

Part 3 of this series will review evidentiary standards for rare diseases. How much is enough?

Presenters

Diane  Berry, PhD

Diane Berry, PhD

Vice President, Global Health Policy and Government Affairs, Sarepta Therapeutics, United States

Diane joined Sarepta as Vice President of Global Health Policy and Government Affairs in 2011. Previously she worked for the federal government, including the Departments of Homeland Security and Defense, overseeing and implementing science and technology and public health activities. Immediately prior to joining Sarepta, Diane served as a Subcommittee Staff Director and Senior Professional Staff Member for the House Committee on Homeland Security.

Alexander  Varond, JD

Alexander Varond, JD

Partner, Goodwin Procter LLP, United States

Alexander J. Varond works on drug development and medical devices, advertising and promotion, and enforcement issues. He counsels clients on drug development matters such as clinical trial design, REMS, orphan drug designation, formal dispute resolution, and patent and exclusivity issues. Mr. Varond also supports ongoing litigation efforts and performs due diligence for corporate transactions.

Patricia  Furlong, BSN

Patricia Furlong, BSN

Founding President and Chief Executive Officer, Parent Project Muscular Dystrophy, United States

Pat Furlong is the Founding President and CEO of Parent Project Muscular Dystrophy (PPMD), the largest nonprofit organization in the United States solely focused on Duchenne muscular dystrophy (Duchenne). Their mission is to end Duchenne. They accelerate research, raise their voices in Washington, demand optimal care for all young men, and educate the global community.

Gerald  Cox, MD, PhD

Gerald Cox, MD, PhD

Chief Medical Officer, Editas Medicine, Inc., United States

Dr. Gerry Cox is Chief Medical Officer at Editas Medicine, a leading genomic medicines company. He was formerly Vice President of Clinical Development for Rare Diseases at Sanofi Genzyme, where for 16 years he oversaw the clinical development programs for several lysosomal storage disorders, including three drug approvals. Dr. Cox is a board-certified clinical geneticist and pediatrician who sees patients part-time at Boston Children’s Hospital, where he was previously on staff and completed his pediatrics and genetics training. He is an instructor in pediatrics at Harvard Medical School. Dr. Cox received a BA in biology from Harvard College in 1980 and an MD, PhD from UCSD in 1989.

Have an account?

Be informed and stay engaged.

Don't miss an opportunity - join our mailing list to stay up to date on DIA insights and events.