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Pediatric Drug Development Workshop

Keynote Address: A Family’s Outlook on the SMA Diagnoses of Their Daughter and Son

Session Chair(s)

Christina Bucci-Rechtweg, MD

Christina Bucci-Rechtweg, MD

  • Global Head, Maternal Health and Pediatric Regulatory Policy
  • Novartis Pharmaceuticals Corporation, United States

Cheryl Yoder will talk about the difference in outlook their family had between the SMA diagnoses of their daughter and son.

The Yoder’s daughter was diagnosed in 2012, at a time when no treatments were on the horizon. Just three years later, in 2015, her son was able to take part in a Phase 2 clinical trial of nusinersen.

Speaker(s)

Cheryl Yoder, RN

Speaker

Cheryl Yoder, RN

  • Patient Advocate
  • Cure SMA, United States

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