戻る Agenda
Gene Therapy – A New Treatment Modality: Opportunities and Challenges from a Patient’s, Industry, Regulatory and Payer’s Perspective
Session Chair(s)
Sam Wadsworth, PHD
Chief Scientific Officer
Dimension Therapeutics, United States
Modifying cellular gene expression to treat diseases has been a long-term goal which, due to novel technologies, now seems to be reachable. The panel will discuss emerging opportunities and hurdles that need to be overcome to make this dream a reality.
Speaker(s)
Gene Therapy- A New Treatment Modality- Opportunities and Challenges from a Regulatory Perspective
Marcel Hoefnagel, DRSC, PHD, MSC
Medicines Evaluation Board , Netherlands
Senior Assessor Biopharmaceuticals
Gene Therapy – The Patient’s Perspective
Dimitrios Athanasiou, MBA
WORLD DUCHENNE ORGANIZATION (WDO) , MDA HELLAS, Greece
Patient Advocate
Challenges in Bringing New Treatment Modalities to Patients
Deya Corzo
UniQure, United States
SVP, Therapeutic Area Head
Adaptive Biomedical Innovation – A Supportive Framework for Accelerating the Development of Gene Therapy Products
Anne-Virginie L. Eggimann, MS
bluebird bio, Inc., United States
Chief Regulatory Offcer