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DIA 2021 Global Annual Meeting


Gene Therapy Research in Pediatric Populations: Ethical Issues

Session Chair(s)

Alison  Bateman-House, PhD, MA, MPH

Alison Bateman-House, PhD, MA, MPH

  • Assistant Professor, Division of Medical Ethics, Dept of Population Health
  • NYU Langone Health, United States
Many gene therapy trials enroll pediatric patients. Clinical research in children raises discrete ethical challenges, as does clinical research involving gene therapy; this forum identifies these challenges and identifies relevant guidance documents.
Learning Objective : Identify the primary ethical challenges facing pediatric gene therapy trials; Assess which ethical challenges are common to all clinical research in children versus which are unique to gene therapy trials in this population; Recognize existing ethical guidance on these issues.

Speaker(s)

Rafael  Escandon, DrPH, PhD, MPH, MS

Panelist

Rafael Escandon, DrPH, PhD, MPH, MS

  • Senior Vice President Medical Affairs, Policy and Patient Engagement
  • Bridgebio Gene Therapy, United States
Alexandra  Hall, MA

Panelist

Alexandra Hall, MA

  • Managing Director: Policy, Patient Support, and Industry
  • The Isaac Foundation, Canada
Lesha D. Shah, MD, FAPA

Panelist

Lesha D. Shah, MD, FAPA

  • Assistant Professor; Medical Director
  • Icahn School of Medicine at Mount Sinai, United States